Research & Innovation

AI in Pediatric Oncology

Artificial intelligence as a decision-support tool alongside the pediatric oncology team.

Artificial intelligence (AI)—including machine learning, deep learning and large-language models—is emerging as an important tool across the pediatric oncology pathway.

AI can help clinicians analyse complex and high-dimensional data from imaging, digital pathology, genomics, electronic health records and treatment response, potentially improving diagnostic accuracy, risk stratification, outcome prediction and treatment selection.

In rare pediatric cancers, where individual centres often have limited datasets, AI may also enable meaningful pattern recognition and collaborative analysis across large multicentre datasets.

Where it is being applied

Emerging applications

Radiomics

Automated pathology interpretation

Molecular classification

Prediction of treatment response and toxicity

Clinical decision support

Identification of potential therapeutic opportunities

What to be careful about

Unique challenges in pediatric oncology

Pediatric oncology presents challenges that general-purpose AI work does not always account for:

  • Small and heterogeneous datasets
  • Limited external validation
  • Algorithmic bias
  • Interpretability
  • Data privacy
  • The need for prospective clinical validation

The guiding principle

AI should be viewed as a decision-support and knowledge-enhancement tool that works alongside the pediatric oncology team, with clinical decisions remaining under expert human oversight.

Published literature

Further reading

1 Hassan M, Shahzadi S, Kloczkowski A. Harnessing Artificial Intelligence in Pediatric Oncology Diagnosis and Treatment: A Review. Cancers, 2025 A very relevant recent review specifically focused on pediatric oncology, including imaging, genomics, radiomics, proteomics and precision medicine. PubMed 2 Elsayid NN et al. The Role of Machine Learning Approaches in Pediatric Oncology: A Systematic Review. Cureus, 2025 Systematically reviews AI/ML studies across hematologic malignancies, solid tumours and CNS tumours, including classification, treatment-response prediction and dose optimisation. PubMed 3 Artificial intelligence applications in pediatric oncology diagnosis. 2023 A useful overview of early applications of AI in pediatric cancer diagnosis, and the specific challenge of limited pediatric datasets. PubMed 4 Making sense of artificial intelligence and large language models — including ChatGPT — in pediatric hematology/oncology. 2024 Particularly relevant for practising pediatric hematologist-oncologists: discusses LLMs, clinical workflow, potential applications, limitations and implementation considerations. PubMed 5 Artificial intelligence in pediatric surgical pathology: A systematic review. Journal of Pediatric Surgery, 2026 Relevant to precision oncology because pathology is increasingly digital and computational. Highlights applications in diagnosis and treatment-response prediction, alongside substantial concerns around validation and bias. ScienceDirect 6 Artificial intelligence in paediatric cancer: Insights from innovation experts in the UNICA4EU project. EJC Paediatric Oncology, 2025 A broader future-of-pediatric-oncology perspective covering tumour screening, imaging, genomics and pathology, and discussing barriers to implementation. ScienceDirect

“The future of pediatric oncology will not be AI versus the clinician—it will be clinicians empowered by AI, molecular data and collaborative intelligence to make better decisions for every child.”